gene therapy

Gene therapy holds promise for treating inherited disorders by correcting defective genes at the source.基因治疗通过在源头上纠正有缺陷的基因，为治疗遗传性疾病带来了希望。

The first approved gene therapy for blindness has restored partial sight in clinical trial participants.首个获批用于治疗失明的基因治疗已使临床试验参与者恢复了部分视力。